Matches in SemOpenAlex for { <https://semopenalex.org/work/W4206155200> ?p ?o ?g. }
- W4206155200 abstract "In vivo genetic engineering has recently shown remarkable potential as a novel effective treatment for an ever-growing number of diseases, as also witnessed by the recent marketing authorization of several in vivo gene therapy products. In vivo genetic engineering comprises both viral vector-mediated gene transfer and the more recently developed genome/epigenome editing strategies, as long as they are directly administered to patients. Here we first review the most advanced in vivo gene therapies that are commercially available or in clinical development. We then highlight the major challenges to be overcome to fully and broadly exploit in vivo gene therapies as novel medicines, discussing some of the approaches that are being taken to address them, with a focus on the nervous system and liver taken as paradigmatic examples." @default.
- W4206155200 created "2022-01-26" @default.
- W4206155200 creator A5020814680 @default.
- W4206155200 creator A5060154023 @default.
- W4206155200 creator A5063249606 @default.
- W4206155200 creator A5066683923 @default.
- W4206155200 date "2022-01-18" @default.
- W4206155200 modified "2023-09-26" @default.
- W4206155200 title "In vivo Gene Therapy to the Liver and Nervous System: Promises and Challenges" @default.
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