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- W4247007757 abstract "The neuromuscular gross motor outcome (GRO) was initially validated to quantify functional change in individuals with spinal muscular atrophy. Previously available tools were developed to measure decline as a result of the untreated natural history. As a result, improvement in function observed with treatment could not be captured on a single scale, limiting the ability to capture longitudinal data as transition to new tests were required as new skills were mastered. The GRO was designed as a single measure to quantify abilities in individuals with very limited movement through more challenging ambulatory activities including running and climbing steps." @default.
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- W4247007757 date "2020-10-01" @default.
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- W4247007757 title "OUTCOME MEASURES" @default.
- W4247007757 doi "https://doi.org/10.1016/j.nmd.2020.08.241" @default.
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