Matches in SemOpenAlex for { <https://semopenalex.org/work/W4280538812> ?p ?o ?g. }
- W4280538812 endingPage "175023" @default.
- W4280538812 startingPage "175023" @default.
- W4280538812 abstract "Gaucher disease (GD), the most common lysosomal disorders, is a rare autosomal recessive hereditary disease that is caused by deficiency of glucosylceramidase. For now, there are five approved therapies for GD, which are used to treat thousands of patients with GD. Despite success of approved therapies, many unresolved issues attract academic institutions and industry to develop potential therapies to resolve them. This paper updated the latest information about approved therapies and potential curative therapies." @default.
- W4280538812 created "2022-05-22" @default.
- W4280538812 creator A5020173957 @default.
- W4280538812 creator A5042026897 @default.
- W4280538812 creator A5050527989 @default.
- W4280538812 creator A5054749361 @default.
- W4280538812 date "2022-07-01" @default.
- W4280538812 modified "2023-09-27" @default.
- W4280538812 title "Update of treatment for Gaucher disease" @default.
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