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- W4308120108 endingPage "6394" @default.
- W4308120108 startingPage "6394" @default.
- W4308120108 abstract "Myasthenia gravis (MG) is a chronic autoimmune disease for which multiple immunomodulatory therapies are available. Nevertheless, MG has a significant impact on patient quality of life. In recent years, experts' main efforts have focused on optimizing treatment strategies, since disease burden is considerably affected by their safety and tolerability profiles, especially in patients with refractory phenotypes. This article aims to offer neurologists caring for MG patients an overview of the most innovative targeted drugs specifically designed for this disease and summarizes the recent literature and more recent evidence on agents targeting B cells and plasmablasts, complement inhibitors, and neonatal fragment crystallizable receptor (FcRn) antagonists. Positive clinical trial results have been reported, and other studies are ongoing. Finally, we briefly discuss how the introduction of these novel targeted immunological therapies in a changing management paradigm would affect not only clinical outcomes, disease burden, safety, and tolerability, but also health spending in a condition that is increasingly managed based on a patient-centred model." @default.
- W4308120108 created "2022-11-08" @default.
- W4308120108 creator A5046280906 @default.
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- W4308120108 creator A5073644680 @default.
- W4308120108 creator A5086490814 @default.
- W4308120108 date "2022-10-28" @default.
- W4308120108 modified "2023-10-18" @default.
- W4308120108 title "New Targeted Agents in Myasthenia Gravis and Future Therapeutic Strategies" @default.
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