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- W4308458520 abstract "Autism spectrum disorder (ASD)-a congenital mental disorder accompanied by social dysfunction and stereotyped behaviors-has attracted a great deal of attention worldwide. A combination of genetic and environmental factors may determine the pathogenesis of ASD. Recent research of multiple ASD models indicates that microRNAs (miRNAs) play a central role at the onset and progression of ASD by repressing the translation of key mRNAs in neural development and functions. As such, miRNAs show great potential to serve as biomarkers for ASD diagnosis or prognosis and therapeutic targets for the treatment of ASD. In this review, we discuss the regulatory mechanisms by which miRNAs influence ASD phenotypes through various in vivo and in vitro models, including necropsy specimens, animal models, cellular models, and, in particular, induced pluripotent stem cells derived from patients with ASD. We then discuss the potential of miRNA-based therapeutic strategies for ASD currently being evaluated in preclinical studies." @default.
- W4308458520 created "2022-11-12" @default.
- W4308458520 creator A5029670581 @default.
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- W4308458520 creator A5086221029 @default.
- W4308458520 date "2022-12-01" @default.
- W4308458520 modified "2023-10-02" @default.
- W4308458520 title "Decoding microRNAs in autism spectrum disorder" @default.
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