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- W4376880237 abstract "Genome engineering technologies provide an entry point into understanding and controlling the function of genetic elements in health and disease. The discovery and development of the microbial defense system CRISPR-Cas yielded a treasure trove of genome engineering technologies and revolutionized the biomedical sciences. Comprising diverse RNA-guided enzymes and effector proteins that evolved or were engineered to manipulate nucleic acids and cellular processes, the CRISPR toolbox provides precise control over biology. Virtually all biological systems are amenable to genome engineering—from cancer cells to the brains of model organisms to human patients—galvanizing research and innovation and giving rise to fundamental insights into health and powerful strategies for detecting and correcting disease. In the field of neuroscience, these tools are being leveraged across a wide range of applications, including engineering traditional and non-traditional transgenic animal models, modeling disease, testing genomic therapies, unbiased screening, programming cell states, and recording cellular lineages and other biological processes. In this primer, we describe the development and applications of CRISPR technologies while highlighting outstanding limitations and opportunities." @default.
- W4376880237 created "2023-05-18" @default.
- W4376880237 creator A5006938194 @default.
- W4376880237 creator A5084006665 @default.
- W4376880237 date "2023-08-01" @default.
- W4376880237 modified "2023-10-09" @default.
- W4376880237 title "CRISPR for neuroscientists" @default.
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