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- W4385740939 abstract "BACKGROUND. Warts, Hypogammaglobulinemia, Infections and Myelokathexis (WHIM) syndrome is a primary immunodeficiency disorder caused by heterozygous gain-of-function CXCR4 mutations. Myelokathexis is neutropenia from neutrophil retention in bone marrow and is associated with lymphopenia and monocytopenia. The CXCR4 antagonist plerixafor mobilizes leukocytes to the blood; however, safety and efficacy in WHIM syndrome are undefined." @default.
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- W4385740939 date "2023-10-02" @default.
- W4385740939 modified "2023-10-04" @default.
- W4385740939 title "A phase 3 randomized crossover trial of plerixafor versus G-CSF for treatment of WHIM syndrome" @default.
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- W4385740939 doi "https://doi.org/10.1172/jci164918" @default.
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