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- W63668720 endingPage "224" @default.
- W63668720 startingPage "189" @default.
- W63668720 abstract "The discovery of RNA interference (RNAi) has transformed molecular biology and offers enormous therapeutic potential. Currently, there are a few approaches to deliver RNAi into cells including the use of a small interfering RNA (siRNA) or a plasmid to express short hairpin RNA (shRNA) or microRNA. Each of these approaches has its advantages and drawbacks. To fully realise the potential of RNAi in clinic, hurdles including specificity, stability and interferon activation of the small RNA need to be overcome. In order to develop RNAi as pharmaceutics for a range of diseases, strategies to deliver the small RNA in specific cell types need to be further developed and refined. In this chapter, the different classes of small RNA, current strategies to overcome therapeutic hurdles and different methods to deliver RNAi are discussed." @default.
- W63668720 created "2016-06-24" @default.
- W63668720 creator A5045547838 @default.
- W63668720 date "2013-01-01" @default.
- W63668720 modified "2023-09-26" @default.
- W63668720 title "The Challenges and Current Advances in Delivering RNAi as Therapeutics" @default.
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