Matches in SemOpenAlex for { <https://semopenalex.org/work/W83040080> ?p ?o ?g. }
Showing items 1 to 71 of
71
with 100 items per page.
- W83040080 endingPage "277" @default.
- W83040080 startingPage "267" @default.
- W83040080 abstract "Access to drugs for rare diseases varies considerably, not only in terms of which drugs are reimbursed but also which patients get access. Five-year-old Luc has been diagnosed with MPS II (Hunter’s Syndrome), a genetic disorder with progressive debilitating symptoms affecting the joints and major organs and, in some children, cognitive functioning. The good news is that there is an approved drug treatment that is effective in “slowing the progression of symptoms”; however, the pivotal clinical trials were only conducted with children over the age of five who had no cognitive impairment. While disease severity is hard to diagnose at an early age, his physician believes Luc has some cognitive impairment. Luc’s ability to get access to treatment depends on where he lives." @default.
- W83040080 created "2016-06-24" @default.
- W83040080 creator A5046538672 @default.
- W83040080 creator A5085523560 @default.
- W83040080 date "2013-10-22" @default.
- W83040080 modified "2023-10-01" @default.
- W83040080 title "Health Policies for Orphan Diseases: International Comparison of Regulatory, Reimbursement and Health Services Policies" @default.
- W83040080 cites W1765989394 @default.
- W83040080 cites W1788182075 @default.
- W83040080 cites W2047591428 @default.
- W83040080 cites W2131080517 @default.
- W83040080 doi "https://doi.org/10.1007/978-3-642-38643-5_27" @default.
- W83040080 hasPublicationYear "2013" @default.
- W83040080 type Work @default.
- W83040080 sameAs 83040080 @default.
- W83040080 citedByCount "3" @default.
- W83040080 countsByYear W830400802018 @default.
- W83040080 countsByYear W830400802021 @default.
- W83040080 countsByYear W830400802023 @default.
- W83040080 crossrefType "book-chapter" @default.
- W83040080 hasAuthorship W83040080A5046538672 @default.
- W83040080 hasAuthorship W83040080A5085523560 @default.
- W83040080 hasConcept C118552586 @default.
- W83040080 hasConcept C126322002 @default.
- W83040080 hasConcept C160735492 @default.
- W83040080 hasConcept C169900460 @default.
- W83040080 hasConcept C17744445 @default.
- W83040080 hasConcept C187212893 @default.
- W83040080 hasConcept C199539241 @default.
- W83040080 hasConcept C2779134260 @default.
- W83040080 hasConcept C2779703844 @default.
- W83040080 hasConcept C2984915365 @default.
- W83040080 hasConcept C535046627 @default.
- W83040080 hasConcept C60644358 @default.
- W83040080 hasConcept C71924100 @default.
- W83040080 hasConcept C75480439 @default.
- W83040080 hasConcept C86803240 @default.
- W83040080 hasConceptScore W83040080C118552586 @default.
- W83040080 hasConceptScore W83040080C126322002 @default.
- W83040080 hasConceptScore W83040080C160735492 @default.
- W83040080 hasConceptScore W83040080C169900460 @default.
- W83040080 hasConceptScore W83040080C17744445 @default.
- W83040080 hasConceptScore W83040080C187212893 @default.
- W83040080 hasConceptScore W83040080C199539241 @default.
- W83040080 hasConceptScore W83040080C2779134260 @default.
- W83040080 hasConceptScore W83040080C2779703844 @default.
- W83040080 hasConceptScore W83040080C2984915365 @default.
- W83040080 hasConceptScore W83040080C535046627 @default.
- W83040080 hasConceptScore W83040080C60644358 @default.
- W83040080 hasConceptScore W83040080C71924100 @default.
- W83040080 hasConceptScore W83040080C75480439 @default.
- W83040080 hasConceptScore W83040080C86803240 @default.
- W83040080 hasLocation W830400801 @default.
- W83040080 hasOpenAccess W83040080 @default.
- W83040080 hasPrimaryLocation W830400801 @default.
- W83040080 hasRelatedWork W2113338089 @default.
- W83040080 hasRelatedWork W2395119479 @default.
- W83040080 hasRelatedWork W2520491083 @default.
- W83040080 hasRelatedWork W2768056166 @default.
- W83040080 hasRelatedWork W2771605862 @default.
- W83040080 hasRelatedWork W3084469869 @default.
- W83040080 hasRelatedWork W4311333739 @default.
- W83040080 hasRelatedWork W4311335622 @default.
- W83040080 hasRelatedWork W4311338524 @default.
- W83040080 hasRelatedWork W4380151265 @default.
- W83040080 isParatext "false" @default.
- W83040080 isRetracted "false" @default.
- W83040080 magId "83040080" @default.
- W83040080 workType "book-chapter" @default.