Matches in SemOpenAlex for { <https://semopenalex.org/work/W876571388> ?p ?o ?g. }
- W876571388 abstract "ABSTRACT In the nearly five decades since its accidental discovery, adeno-associated virus (AAV) has emerged as a highly versatile vector system for both research and clinical applications. A broad range of natural serotypes, as well as an increasing number of capsid variants, has combined to produce a repertoire of vectors with different tissue tropisms, immunogenic profiles and transduction efficiencies. The story of AAV is one of continued progress and surprising discoveries in a viral system that, at first glance, is deceptively simple. This apparent simplicity has enabled the advancement of AAV into the clinic, where despite some challenges it has provided hope for patients and a promising new tool for physicians. Although a great deal of work remains to be done, both in studying the basic biology of AAV and in optimizing its clinical application, AAV vectors are currently the safest and most efficient platform for gene transfer in mammalian cells." @default.
- W876571388 created "2016-06-24" @default.
- W876571388 creator A5020081853 @default.
- W876571388 creator A5044065218 @default.
- W876571388 creator A5050777934 @default.
- W876571388 date "2015-07-02" @default.
- W876571388 modified "2023-09-30" @default.
- W876571388 title "Adeno-associated Virus as a Mammalian DNA Vector" @default.
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